Capito, Stabenow, Roskam, Sánchez Introduce Bill to Improve Assessment, Diagnosis of Alzheimer’s Rebecca BallietFebruary 8, 2018
Rare pediatric disease designation awarded to sickle cell treatment Rebecca BallietSeptember 21, 2017
Imara Receives Rare Pediatric Disease Designation from FDA for Lead Product Candidate IMR-687 for Sickle Cell Disease Rebecca BallietMay 15, 2017
Signing of ‘Cures Act’ Welcomed for Potential in Speeding New Sickle Cell Treatments Rebecca BallietDecember 20, 2016
Agilis Biotherapeutics Achieves FDA “Rare Pediatric Disease” Designation for AADC Gene Therapy Candidate Rebecca BallietNovember 17, 2016
